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Q&A: One scientist’s bold vision to make on-demand treatments routine for life-threatening rare genetic diseases

Broad Institute

Indeed, in 2022 Alyssa Tapley became the first human to receive a base-edited therapeutic, treating her life-threatening T-cell leukemia that had not responded to other treatments. Together, base editing and prime editing technologies provide powerful tools to bring genetic treatments to more patients.

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A Visual Guide to Genome Editors

Codon

pyogenes protein — whose compactness makes them far easier to package into viral vectors and deliver into the human body. Therapeutics Verve Therapeutics began the first clinical trial using base editors in 2022, with the goal of treating genetic contributors to heart disease.

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Case study: gget’s new Open Target module

The Open Targets Blog

gget ( [link] ) is a free, open-source command-line tool and Python package designed to enable efficient querying of large genomic databases, such as Ensembl, UniProt, and NCBI. We chatted to the team about the module, and how it facilitates access to Open Targets Platform data. What is gget?

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The Uncertain Origins of Aspirin

Codon

Eichengrün noted that it wasn’t just that aspirin was effective with limited side effects, but also that it came packaged as tablets rather than as a powder in a paper bag. 2 Accurate global statistics are difficult (possibly impossible) to find for the total number of prescribed NSAIDs, but in 2022 in the U.S., million).

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Key Insights from the Front-End Meetup by the Front-End Meetup Group

Perficient: Drug Development

Rajiv’s session focused on Docker, explaining how it allows developers to package, deploy, and run applications in isolated containers, ensuring consistency across different environments. Achievements: Best Coder Award 2019 (Smart Data Enterprises) and 2022 (HCLTech). Best Trainer in Data Analytics Arc Technologies.

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AZVUDINE

New Drug Approvals

8] It costs 350 Chinese yuan per 7 days for COVID, as of November 2022. [9] SYN [link] Azvudine was approved for the treatment of adult HIV-1 infection in China in 2021, and it was approved for conditional marketing for the treatment of SARS-CoV-2 in China in 2022. 2022, 55, 565−578. (8) 2020, 63, 8554−8566. (7) 7) Chang, J.

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Pharmaceutical Manufacturing And Packaging Congress 2022 Connects Pharma Leaders

The Pharma Data

Pharmaceutical Manufacturing & Packaging Congress (PHARMAP 2022) covers the current state of the pharmaceutical manufacturing and packaging industry. It takes place on June, 20-21, 2022 in Berlin, Germany. It takes place on June, 20-21, 2022 in Berlin, Germany.