Q&A: One scientist’s bold vision to make on-demand treatments routine for life-threatening rare genetic diseases
Broad Institute
JUNE 24, 2025
Together, these technologies have entered at least 19 clinical trials, with clinical results from seven of those trials reported so far — all showing that the base edit or prime edit resulted in patient benefit. Of the 19 base editing and prime editing clinical trials underway now, more are taking place outside the U.S.
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