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How AI will reshape pharma by 2025

Drug Target Review

” Weve definitely come across people in the pharma industry who worry that AI means companies might steal our data or use it in harmful ways. Smith states, weve definitely come across people in the pharma industry who worry that AI means companies might steal our data or use it in harmful ways.

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The rising impact of biomarkers in early clinical development

Drug Target Review

For example, transcriptomic processes are showing the potential to identify and track failures in gene expression and gene regulation of amyloid and tau-related biomarkers, understood as precursors to the onset of Alzheimers disease (AD). Transcriptomics in Alzheimers Disease: Aspects and Challenges. 21(10):3517. Rodrigues AD.

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7 Steps to Define a Data Governance Structure for a Mid-Sized Bank (Without Losing Your Mind)

Perficient: Drug Development

Establish a single source of truth Create a glossary that doesn’t read like a legal document Accept that these definitions will change more often than a teenager’s social media profile It’s not perfect, but it’s governance, not a philosophical treatise on the nature of reality. So very, very wrong.

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The future of CNS drug development: signs of real progress

Drug Target Review

Developers and sponsors working on biologically derived therapies in the US can utilise the Regenerative Medicine Advanced Therapy (RMAT) designation, which regulators grant to promising regenerative therapies. The blood–brain barrier: Structure, regulation and drug delivery. Adv Drug Deliv Rev. 2020;165-166:1-14. doi: 10.1016/j.addr.2019.11.009.

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Overcoming Orphan Drug Development Challenges with Real-World Data and Evidence

PPD

While there is no universally accepted definition for rare disease, it is estimated that more than 10,000 distinct rare conditions exist, and people living with these rare diseases represent as much as 10% of the global population. In rare diseases, evidence gaps are often significant, necessitating de novo evidence generation.

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BioMarin Completes Acquisition of Inozyme Pharma

The Pharma Data

INZ-701 is designed to replace deficient ENPP1 enzyme activity, with the aim of restoring normal regulation of mineralization processes in the body. Timeline of the Transaction The acquisition process began on May 16, 2025, when BioMarin and Inozyme jointly announced the signing of a definitive merger agreement. per share.

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Spirulina’s role in shaping the future of preventative biologics

Drug Target Review

By definition, preventative drugs are taken by a larger number of customers because you never know exactly whos going to get an infection its probabilistic. Preventative drugs, unlike antibiotics used to treat infections, are taken proactively, which opens a broader market.