Drugs.com

DECEMBER 8, 2023

Food and Drug Administration on Friday approved two milestone gene therapies for sickle cell disease, including the first treatment ever approved that uses gene-editing technology. FRIDAY, Dec. 8, 2023 -- The U.S. Casgevy, developed by Vertex.

FDA Approval 312

FDA Approval Therapies FDA Treatment 312

Drugs.com

OCTOBER 22, 2024

22, 2024 -- At-home brain stimulation therapy can safely and effectively treat severe to moderate depression, a new clinical trial shows.Rates of treatment response and depression remission were three times higher in people receiving. TUESDAY, Oct.

Treatment 279

Treatment Clinical Trials Therapies Trials 279

Drugs.com

JANUARY 24, 2024

Food and Drug Administration has told drugmakers to add a boxed warning to a type of cancer treatment called CAR-T therapy, saying the treatment itself may sometimes cause a secondary. WEDNESDAY, Jan. 24, 2024 (Healthday News) -- The U.S.

Therapies 306

Therapies FDA Treatment Drugs 306

Drugs.com

OCTOBER 22, 2024

22, 2024 -- Light therapy could be a useful treatment for the most common form of age-related macular degeneration, a new study says.The therapy, called photobiomodulation or “red light” therapy, can reduce the risk of vision loss and. TUESDAY, Oct.

Therapies 264

Therapies Treatment 264

Drugs.com

SEPTEMBER 26, 2024

25, 2024 -- A new gene therapy approved earlier this year can serve as a sustainable single-dose treatment for people with hemophilia B, newly published clinical trial data shows. THURSDAY, Sept. People with hemophilia B saw their bleeding episodes.

Therapies 290

Therapies Trials Clinical Trials Treatment 290

Science Daily: Pharmacology News

FEBRUARY 11, 2025

Scientists have developed new light-sensitive chemicals that can radically improve the treatment of aggressive cancers with minimal side effects. In mouse tests, the new therapy completely eradicated metastatic breast cancer tumors.

Treatment 269

Treatment Therapies 269

BioPharma Drive: Drug Pricing

MAY 22, 2025

Still, the therapies’ modest benefit as a maintenance therapy points to how better treatments are needed for small cell lung cancer, according to one physician.

Therapies 272

Therapies Treatment 272

Drugs.com

JUNE 18, 2024

TUESDAY, June 18, 2024 -- There's more good news in the battle against sickle cell disease, with another trial finding CRISPR gene-editing therapy delivering impressive results for patients.“It’s It’s encouraging that this gene-editing treatment con.

Therapies 264

Therapies Trials Treatment Disease 264

Drugs.com

SEPTEMBER 11, 2024

11, 2024 -- Contrary to a warning placed on labels for CART-T cancer therapies, use of these treatments does not appear to boost the odds for a secondary cancer later, a new study shows.Researchers at Memorial Sloan Kettering. WEDNESDAY, Sept.

Therapies 279

Therapies Treatment 279

BioPharma Drive: Drug Pricing

JANUARY 26, 2024

The opinion would allow Abecma to be prescribed after two standard therapies and is the latest sign of CAR-T’s growing use in earlier cancer treatment.

Therapies 301

Therapies Treatment 301

Drugs.com

MAY 17, 2024

FRIDAY, May 17, 2024 -- Cutting-edge cancer treatments are essentially useless for patients barely clinging to life, a new study shows.Chemotherapies, immunotherapies, targeted therapies and hormone therapies do not improve survival rates in.

Treatment 278

Treatment Therapies 278

Chemical Biology and Drug Design

MAY 12, 2025

CRISPR-CAS9 is an innovative gene editing technology to precisely remove or incorporate into the gene of interest; CRISPR-CAS9 shows promising results in HIV treatment. This article outlines the current antiretroviral therapy and its adverse effects but also CRISPR/Cas technology.

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Treatment Therapies DNA RNA 100

Drugs.com

JUNE 23, 2023

Food and Drug Administration on Thursday approved the drug Elevidys, the first gene therapy for the treatment of children with Duchenne muscular dystrophy (DMD). The groundbreaking treatment will not be cheap: FRIDAY, June 23, 2023 -- The U.S.

FDA Approval 278

FDA Approval Therapies FDA Treatment 278

BioPharma Drive: Drug Pricing

AUGUST 24, 2023

The deal, worth up to $500 million, is a bet by the drug rights dealmaker on the uncertain commercial prospects of Ferring's gene therapy Adstiladrin.

Therapies 244

Therapies Treatment Drugs 244

BioPharma Drive: Drug Pricing

OCTOBER 5, 2023

Kyowa will pay nearly $400 million to acquire Orchard, which sells the gene therapy Libmeldy in Europe but has struggled to find paths to market for other experimental treatments.

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Therapies Treatment Marketing 273

Drug Target Review

JUNE 9, 2025

“This experience underscored the gaps in rare disease innovation, motivating me to lead Alltrna, a company pioneering engineered tRNA therapies to address a broad range of genetic diseases in a profound way unlike any other genetic modality.”

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Disease Treatment Engineering Protein Production 80

BioPharma Drive: Drug Pricing

JUNE 27, 2023

The treatment could become Pfizer’s first marketed gene therapy, an area the pharma has poured significant resources into in recent years.

Therapies 274

Therapies Treatment Marketing 274

BioPharma Drive: Drug Pricing

JANUARY 24, 2024

An 11-year-old boy born deaf can hear after receiving Lilly's genetic medicine. Others, including biotechs in China and Regeneron in the U.S., are taking aim at the same drug target.

Therapies 300

Therapies Treatment Drugs 300

BioPharma Drive: Drug Pricing

FEBRUARY 21, 2024

One expert views Amtagvi’s approval as a catalyst for further investment in TIL therapies, akin to how Kymriah’s 2017 clearance buoyed CAR-T treatment.

FDA Approval 277

FDA Approval Therapies FDA Treatment 277

Drugs.com

APRIL 1, 2024

MONDAY, April 1, 2024 -- Telehealth might be a more effective way of treating alcoholism than in-person therapy sessions, a new study reports.Alcoholics who receive treatment through telehealth were more likely to engage in more therapy visits and.

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Treatment Therapies 245

Drugs.com

SEPTEMBER 26, 2024

25, 2024 -- A new gene therapy approved earlier this year can serve as a sustainable single-dose treatment for people with hemophilia B, newly published clinical trial data shows.People with hemophilia B saw their bleeding episodes. THURSDAY, Sept.

Therapies 246

Therapies Trials Clinical Trials Treatment 246

BioPharma Drive: Drug Pricing

JUNE 3, 2025

Elinzanetant proved effective for managing disruptive vasomotor symptoms in women on endocrine therapy, supporting a Bayer application for approval.

Treatment 216

Treatment Therapies Drugs 216

Science Daily: Pharmacology News

DECEMBER 8, 2023

A landmark study has shown that severe asthma can be controlled using biologic therapies, without the addition of regular high-dose inhaled steroids which can have significant side effects.

Treatment 309

Treatment Therapies 309

Drugs.com

DECEMBER 8, 2023

Food and Drug Administration on Friday approved two milestone gene therapies for sickle cell disease, including the first treatment ever approved that uses gene-editing technology.Casgevy, developed by Vertex. FRIDAY, Dec. 8, 2023 -- The U.S.

FDA Approval 246

FDA Approval Therapies FDA Treatment 246

Drugs.com

JUNE 23, 2023

Food and Drug Administration on Thursday approved the drug Elevidys, the first gene therapy for the treatment of children with Duchenne muscular dystrophy (DMD). The groundbreaking treatment will not be cheap: FRIDAY, June 23, 2023 -- The U.S.

FDA Approval 246

FDA Approval Therapies FDA Treatment 246

BioPharma Drive: Drug Pricing

FEBRUARY 25, 2025

Ten of 11 children born with a rare form of congenital hearing loss experienced improvements after receiving the company’s treatment, new data show.

Therapies 325

Therapies Treatment 325

BioPharma Drive: Drug Pricing

SEPTEMBER 5, 2023

The FDA-approved therapy, called Palforzia, was little used, leading Nestle to abandon a business it had secured in a $2.6 billion deal three years ago.

FDA Approval 326

FDA Approval Treatment FDA Therapies 326

Drugs.com

JULY 13, 2023

THURSDAY, July 13, 2023 -- A preclinical study offers a potential new therapy for treatment-resistant prostate cancer, offering new hope for men with the disease. The study used the chemotherapy drug cisplatin, administered orally, to disrupt the.

Treatment 246

Treatment Therapies Disease Drugs 246

Drugs.com

JUNE 14, 2024

FRIDAY, June 14, 2024 -- Animal studies are often considered a first step in finding new drugs and treatments for human diseases, but a new review has discovered that precious few actually produce real-world therapies. Only 5% of therapies tested.

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Treatment Therapies Disease Drugs 246

Drugs.com

APRIL 1, 2024

MONDAY, April 1, 2024 -- A monthly long-acting injection of buprenorphine can be an easier and more effective therapy for people struggling with opioid addiction, but treatment centers aren’t much interested in using it, a new study.

Treatment 246

Treatment Therapies 246

BioPharma Drive: Drug Pricing

OCTOBER 31, 2023

The high-profile meeting focused on the theoretical risks of CRISPR gene editing, as both the FDA and its advisory committee appeared convinced by the efficacy of the companies’ exa-cel treatment.

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FDA Therapies Treatment 337

Drugs.com

JUNE 27, 2024

THURSDAY, June 27, 2024 -- Acupuncture can help breast cancer patients deal with the hot flashes that often accompany hormone therapy, a new clinical trial says.Nearly 2 in 3 women who got acupuncture during hormone therapy reported fewer and less.

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Clinical Trials Treatment Therapies Trials 263

Science Daily: Pharmacology News

APRIL 2, 2025

The treatment method restores vision through retinal nerve regeneration. Researchers have successfully developed a novel drug to restore vision.

Therapies 267

Therapies Treatment Research Drugs 267

Drugs.com

AUGUST 14, 2023

14, 2023 -- For people with severe alcohol use disorder, a new gene therapy trial could lead to an effective treatment that would involve chemically rebalancing the area of the brain associated with addiction. MONDAY, Aug. With alcohol alone,

Therapies 246

Therapies Trials Treatment 246

BioPharma Drive: Drug Pricing

DECEMBER 8, 2023

In addition to clearing Vertex Pharmaceuticals and CRISPR Therapeutics’ Casgevy, the FDA also granted an early OK to Bluebird bio’s sickle cell treatment Lyfgenia.

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FDA Therapies Pharmaceuticals Treatment 349

Drugs.com

JUNE 7, 2023

TUESDAY, June 6, 2023 -- Radiation therapy might not be necessary in treating some forms of rectal cancer and lymphoma, sparing patients from the toxic treatment, a pair of new clinical trials shows. One trial found that rectal cancer patients.

Therapies 246

Therapies Clinical Trials Trials Treatment 246

Drugs.com

APRIL 21, 2025

MONDAY, April 21, 2025 -- Chris Vogelsang has had a long and terrible fight with cancer. Fourteen years ago, the 70-year-old man was first diagnosed with an aggressive form of lymphoma. His cancer has since returned twice, fighting against several.

Therapies 257

Therapies Treatment 257