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FDA Approves Landmark Sickle Cell Gene Therapies, Casgevy and Lyfgenia

Drugs.com

8, 2023 -- The U.S. Food and Drug Administration on Friday approved two milestone gene therapies for sickle cell disease, including the first treatment ever approved that uses gene-editing technology. FRIDAY, Dec. Casgevy, developed by Vertex.

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Could 'Float Therapy' Help Ease Anorexia?

Drugs.com

1, 2023 -- Float therapy, where a patient is suspended in a pool of warm, salty water in a soundproof room, could help ease some aspects of anorexia nervosa, a small new study found. FRIDAY, Sept. The idea is that women with anorexia have.

Therapies 264
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FDA Approves First Gene Therapy, Elevidys, to Treat Duchenne Muscular Dystrophy

Drugs.com

FRIDAY, June 23, 2023 -- The U.S. Food and Drug Administration on Thursday approved the drug Elevidys, the first gene therapy for the treatment of children with Duchenne muscular dystrophy (DMD). The groundbreaking treatment will not be cheap:

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More Evidence Gene Therapy Might Cure Sickle Cell Disease

Drugs.com

MONDAY, June 12, 2023 -- A clinical trial that’s attempting to discover a cure for sickle cell disease has found a new gene therapy to be safe and successful in four patients. Two of the patients were treated at Cleveland Clinic Children’s in.

Therapies 264
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Experimental Therapy Eases Alzheimer's Signs, Symptoms in Mice

Drugs.com

29, 2023 -- A new cellular therapy improved learning and memory in mice with Alzheimer's disease, researchers report.The therapy -- developed at the University of Nebraska Medical Center (UNMC) -- relies on both the immune system to. FRIDAY, Dec.

Therapies 244
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FDA Approves Landmark Sickle Cell Gene Therapies

Drugs.com

8, 2023 -- The U.S. Food and Drug Administration on Friday approved two milestone gene therapies for sickle cell disease, including the first treatment ever approved that uses gene-editing technology.Casgevy, developed by Vertex. FRIDAY, Dec.

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In Mice, Gene Therapy Helps Restore Movement After Spinal Cord Injury

Drugs.com

27, 2023 -- Gene therapy has restored mobility in mice with completely severed spinal cords, researchers report. WEDNESDAY, Sept. The mice regained the ability to walk, with gait patterns resembling those of mice that resumed walking naturally after.

Therapies 262