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Genomic score predicts patients' progression to multiple myeloma

Broad Institute

Adelson Medical Research Foundation, the International Myeloma Society, Dana-Farber Cancer Institute, the Krouse Family Foundation, the National Cancer Institute, and Stand Up to Cancer. These insights wouldn't be possible without access to deeply sequenced whole genomes from a large number of patients and across different disease stages."

DNA
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Alnylam Promotes Pushkal Garg to Chief R&D Officer

The Pharma Data

Following his residency in Internal Medicine at UCSF, Dr. Garg was selected as a fellow in the prestigious Robert Wood Johnson Clinical Scholars Program at Johns Hopkins University. He holds a B.A. in Biochemistry with high honors from the University of California, Berkeley, and earned his medical degree (M.D.)

RNA
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FDA Approves Merck’s ENFLONSIA™ to Prevent RSV in Infants

The Pharma Data

The Urgent Need for RSV Prevention in Infants Respiratory syncytial virus is the leading cause of infant hospitalizations in the United States, and it is known to trigger severe respiratory illnesses such as bronchiolitis and pneumonia in young children. RSV disease is the leading cause of infant hospitalization in the U.S.

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Biogen Shares Promising Nusinersen Data in Continued Mission to Improve Lives of Those with

The Pharma Data

With regulatory applications for a higher-dose regimen of nusinersen currently under review in the United States, Europe, Japan, and other international markets, Biogen is signaling a continued commitment to refining and optimizing care for individuals living with SMA. Jude Children’s Research Hospital.

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AC102 Eliminates Tinnitus in Preclinical Study

The Pharma Data

The results, recently published in the International Journal of Molecular Sciences , come from a collaborative effort between researchers at Erlangen University Hospital and Berlin-based biotech firm AudioCure. These findings are particularly relevant in the context of sudden hearing loss, a condition often accompanied by tinnitus.

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FDA Grants Accelerated Approval to Lynozyfic™ for Relapsed or Refractory Multiple Myeloma

The Pharma Data

The regimen includes mandatory hospitalization for 24 hours following each of the first two step-up doses, a precaution to manage cytokine release syndrome (CRS) and other adverse reactions. Diane Moran, Interim CEO of the International Myeloma Foundation, remarked, “Even with recent treatment advances, multiple myeloma remains incurable.

FDA
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Sanofi Speeds Up Beyfortus Shipments Ahead of 2025-2026 RSV Season

The Pharma Data

RSV is the leading cause of lower respiratory tract disease and a top reason for hospitalization among infants. Importantly, most RSV-related hospitalizations occur in healthy, full-term infants who previously showed no signs of underlying health conditions.